Active	Status	Sponsor type	Region	Phase	Filter
2 Active 0 Inactive 2 All	Not yet recruiting Recruiting Enrolling by invitation Active, not recruiting Available No longer recruiting	Industry lead sponsor Industry collaborator Coop Other	US Canada Japan Europe RoW	N/A 1 2 3 4	Highlight changes:- Show only changed items Enrollment:

Advanced Filters

2 Trials

Active Trials   

 

Export

Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Lachmann, Robin
NCT05526066 / 2021-001081-38: Study for Adolescents and Adults With Ornithine Transcarbamylase Deficiency to Evaluate Safety and Tolerability of ARCT-810	Active, not recruiting	2	24	Europe	ARCT-810, Placebo	Arcturus Therapeutics, Inc., Arcturus Therapeutics, Inc.	Ornithine Transcarbamylase Deficiency, OTC Deficiency, OTCD	12/24	03/25
Gaucherite, NCT03240653: - A Study to Stratify Gaucher Disease	Recruiting	N/A	250	Europe	Stratified response to Enzyme Therapy, Stratified response to Substrate Reduction Therapy, Splenectormy	Cambridge University Hospitals NHS Foundation Trust, Medical Research Council, National Institute for Health Research, United Kingdom	Gaucher Disease, Type I, Gaucher Disease, Type III	09/28	12/28