Shneider, Benjamin |
NCT02055768: Safety and Efficacy Study of the Intestinal Bile Acid Transport (IBAT) in the Reduction of Pruritus in ALGS |
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| Not yet recruiting | 2 | 24 | US, Canada | LUM001 70 ug/kg/day, Intestinal Bile Acid Transport (IBAT) Inhibitor, Placebo, LUM001 140 ug/kg/day | National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK), Lumena Pharmaceuticals, Inc. | Pruritus, Alagille Syndrome | 02/15 | 05/15 | | |
NCT02922751: FibroScan™ in Pediatric Cholestatic Liver Disease (FORCE) |
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| Completed | N/A | 552 | Canada, US | Liver Stiffness Measurement (LSM), FibroScan™ | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Biliary Atresia, Alagille Syndrome, Alpha1 Anti-Trypsin Deficiency, Portal Hypertension, Liver Fibrosis, Cholestasis | 12/22 | 12/22 | | |
| Recruiting | N/A | 1000 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Biliary Atresia, Neonatal Cholestasis | 05/29 | 05/29 | | |
| Recruiting | N/A | 1265 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Biliary Atresia | 05/29 | 05/29 | | |
| Suspended | N/A | 1675 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Liver Diseases, Alagille Syndrome, Alpha 1-Antitrypsin Deficiency | 05/29 | 05/29 | | |
| Suspended | N/A | 67 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK), University of Michigan | Acute Liver Failure, Mitochondrial Diseases, End Stage Liver Disease, Respiratory Chain Deficiencies, Mitochondrial, Disorder of Fatty Acid Oxidation | 05/29 | 05/29 | | |
| Recruiting | N/A | 2230 | Canada, US | | Arbor Research Collaborative for Health | Liver Diseases | 05/29 | 05/29 | | |
Cavallo, Laurel |
| Recruiting | N/A | 1000 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Biliary Atresia, Neonatal Cholestasis | 05/29 | 05/29 | | |
| Recruiting | N/A | 1265 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Biliary Atresia | 05/29 | 05/29 | | |
| Suspended | N/A | 1675 | Canada, US | | Arbor Research Collaborative for Health, National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK) | Liver Diseases, Alagille Syndrome, Alpha 1-Antitrypsin Deficiency | 05/29 | 05/29 | | |
| Recruiting | N/A | 2230 | Canada, US | | Arbor Research Collaborative for Health | Liver Diseases | 05/29 | 05/29 | | |