| Recruiting | N/A | 2000 | Europe | | University of Bern, University Children's Hospital Basel, Insel Gruppe AG, University Hospital Bern, University of Lausanne Hospitals, Ente Ospedaliero Cantonale, Bellinzona, University Children's Hospital, Zurich | SMA, DMD, BMD, IMD, Congenital Muscular Dystrophy | 01/71 | 01/71 | | |