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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Longo, Nichola
NCT05099640 / 2021-000474-29: A Study of PTC923 in Participants With Phenylketonuria	Completed	3	157	Europe, Canada, US, RoW	PTC923, Placebo	PTC Therapeutics	Phenylketonuria	04/23	05/23
NCT05166161 / 2021-000497-28: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria	Recruiting	3	200	Europe, Canada, Japan, US, RoW	PTC923, Sepiapterin	PTC Therapeutics	Phenylketonuria	04/26	04/26
Tchan, Michel
NCT05099640 / 2021-000474-29: A Study of PTC923 in Participants With Phenylketonuria	Completed	3	157	Europe, Canada, US, RoW	PTC923, Placebo	PTC Therapeutics	Phenylketonuria	04/23	05/23
NCT05166161 / 2021-000497-28: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria	Recruiting	3	200	Europe, Canada, Japan, US, RoW	PTC923, Sepiapterin	PTC Therapeutics	Phenylketonuria	04/26	04/26
CACN00177-100D, NCT05154890 / 2019-004791-19: A Multiple Ascending Dose Study of ACN00177 (Pegtarviliase) in Subjects With CBS Deficiency	Terminated	1/2	13	Europe, US, RoW	Pegtarviliase IV, ACN00177, Pegtarviliase SC	Aeglea Biotherapeutics, Aeglea Biotherapeutics	Homocystinuria Due to Cystathionine Beta-Synthase Deficiency	04/23	04/23