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Trial + Data / Events	Status	Ph	N	Region	Interventions	Sponsor	Conditions	Primary compl	Study compl
Zori, Roberto
NCT03335488 / 2015-000075-27: Study of Glycerol Phenylbutyrate & Sodium Phenylbutyrate in Phenylbutyrate Naïve Patients With Urea Cycle Disorders (UCDs)	Completed	4	16	Europe, US	RAVICTI, Glycerol phenylbutyrate, GPB, HPN-100, NaPBA, Sodium phenylbutyrate	Amgen	Urea Cycle Disorder	07/22	12/22
NCT05099640 / 2021-000474-29: A Study of PTC923 in Participants With Phenylketonuria	Completed	3	157	Europe, Canada, US, RoW	PTC923, Placebo	PTC Therapeutics	Phenylketonuria	04/23	05/23
SYNPHENY-3, NCT05764239: Efficacy and Safety of SYNB1934 in Patients With PKU	Terminated	3	35	Canada, US, RoW	SYNB1934v1, Placebo	Synlogic	Phenylketonuria	03/24	03/24
NCT05166161 / 2021-000497-28: A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria	Recruiting	3	200	Europe, Canada, Japan, US, RoW	PTC923, Sepiapterin	PTC Therapeutics	Phenylketonuria	04/26	04/26
NCT05781399: First-in-Human, Multiple Part Clinical Study of JNT-517 in Healthy Participants and in Participants With Phenylketonuria	Recruiting	1	112	US, RoW	JNT-517 Suspension, Placebo Suspension, JNT-517 Tablet, Placebo Tablet	Jnana Therapeutics	Phenylketonuria	12/24	03/25