- |||||||||| Trial completion date, Trial primary completion date: Genetics of Cardiovascular and Neuromuscular Disease (clinicaltrials.gov) - Jul 25, 2024
P=N/A, N=2000, Recruiting, Trial completion date: Jan 2025 --> Jan 2026 | Trial primary completion date: Jan 2025 --> Jan 2026
- |||||||||| Trial completion, Enrollment change, Trial primary completion date: STEADFAST: Stacking Exercises Aid the Decline in FVC and Sick Time (clinicaltrials.gov) - Dec 24, 2018
P4, N=70, Completed, Trial completion date: Jan 2025 --> Jan 2026 | Trial primary completion date: Jan 2025 --> Jan 2026 Active, not recruiting --> Completed | N=110 --> 70 | Trial primary completion date: Aug 2018 --> Nov 2018
- |||||||||| NN1213 / Novo Nordisk
Enrollment change, Trial withdrawal: Cell Therapy in Limb Girdle Muscular Dystrophy (clinicaltrials.gov) - Oct 25, 2018 P1, N=0, Withdrawn, Active, not recruiting --> Completed | N=110 --> 70 | Trial primary completion date: Aug 2018 --> Nov 2018 N=65 --> 0 | Completed --> Withdrawn
- |||||||||| NN1213 / Novo Nordisk
Enrollment change, Trial withdrawal: Stem Cell Therapy in Duchenne Muscular Dystrophy (clinicaltrials.gov) - Oct 25, 2018 P1, N=0, Withdrawn, N=65 --> 0 | Completed --> Withdrawn N=245 --> 0 | Completed --> Withdrawn
- |||||||||| NN1213 / Novo Nordisk
Enrollment change, Trial withdrawal: Stem Cell Therapy in Muscular Dystrophy (clinicaltrials.gov) - Oct 25, 2018 P1, N=0, Withdrawn, N=245 --> 0 | Completed --> Withdrawn N=1000 --> 0 | Recruiting --> Withdrawn
- |||||||||| lisinopril / Generic mfg.
Trial completion, Enrollment change: Clinical Trial of Coenzyme Q10 and Lisinopril in Muscular Dystrophies (clinicaltrials.gov) - Jun 15, 2018 P2/3, N=63, Completed, Trial completion date: Mar 2012 --> Mar 2016 | Trial primary completion date: Mar 2012 --> Mar 2016 Enrolling by invitation --> Completed | N=120 --> 63
- |||||||||| Trial completion date, Trial primary completion date: Stem Cell Therapy in Muscular Dystrophy (clinicaltrials.gov) - Mar 30, 2018
P1, N=1000, Recruiting, Phase classification: P=N/A --> P Trial completion date: May 2018 --> May 2019 | Trial primary completion date: Dec 2017 --> Dec 2018
- |||||||||| Trial completion: DM1: Arrhythmias in Myotonic Muscular Dystrophy (clinicaltrials.gov) - Feb 14, 2018
P=N/A, N=448, Completed, Recruiting --> Completed | Trial completion date: Feb 2028 --> Nov 2017 | Trial primary completion date: Feb 2020 --> Nov 2017 Active, not recruiting --> Completed
- |||||||||| Trial completion, Trial primary completion date, HEOR: A Multicenter Collaborative Study on the Clinical Features, Expression Profiling, and Quality of Life of Infantile Onset FSHD (clinicaltrials.gov) - Oct 11, 2017
P=N/A, N=53, Completed, Active, not recruiting --> Completed Active, not recruiting --> Completed | Trial primary completion date: Aug 2018 --> Aug 2017
- |||||||||| Enrollment status, Trial primary completion date, HEOR: Duchenne Muscular Dystrophy < 18y in Norway: Genotype/Phenotype, Growth, Puberty, Bone Health and Quality of Life. (clinicaltrials.gov) - Apr 7, 2017
P=N/A, N=70, Enrolling by invitation, Active, not recruiting --> Completed Recruiting --> Enrolling by invitation | Trial primary completion date: Dec 2016 --> Jun 2017
- |||||||||| Trial completion, Phase classification, Trial initiation date: Efficacy and Tolerance of AVAPS Mode in Myotonic Dystrophy (clinicaltrials.gov) - Mar 10, 2017
P=N/A, N=32, Completed, Recruiting --> Enrolling by invitation | Trial primary completion date: Dec 2016 --> Jun 2017 Recruiting --> Completed | Phase classification: P4 --> PN/A | Initiation date: Feb 2011 --> Jul 2012
- |||||||||| Biomarker, Enrollment closed, Enrollment change, Trial primary completion date: MOS-DM1/POP: Multicenter Observational Study of Myotonic Dystrophy Type 1 (clinicaltrials.gov) - Mar 1, 2017
P=N/A, N=120, Active, not recruiting, Recruiting --> Completed | Phase classification: P4 --> PN/A | Initiation date: Feb 2011 --> Jul 2012 Recruiting --> Active, not recruiting | N=100 --> 120 | Trial primary completion date: Dec 2015 --> Jul 2017
- |||||||||| Enrollment closed, Enrollment change: Whole Body Vibration Therapy in Boys With Duchenne Muscular Dystrophy (clinicaltrials.gov) - Feb 23, 2017
P=N/A, N=4, Active, not recruiting, Recruiting --> Active, not recruiting | N=100 --> 120 | Trial primary completion date: Dec 2015 --> Jul 2017 Recruiting --> Active, not recruiting | N=20 --> 4
- |||||||||| Kyndrisa (drisapersen) / BioMarin
Trial termination, Trial primary completion date: A Phase I/II, Open Label, Escalating Dose, Pilot Study to Assess Effect, Safety, Tolerability and PK of Multiple SC Doses of Drisapersen in Patients With Duchenne Muscular Dystrophy and to Assess the Potential for IV Dosing as an Alternative Route of Administration (clinicaltrials.gov) - Nov 7, 2016 P2, N=12, Terminated, Recruiting --> Completed | N=50 --> 38 | Trial primary completion date: Jun 2015 --> Jan 2015 Active, not recruiting --> Terminated | Trial primary completion date: May 2009 --> Sep 2016; Regulatory approval was not obtained for drisapersen, hence BioMarin is stopping the development of all exon skipping oligonucleotides in DMD.
- |||||||||| BMN 045 / BioMarin
Enrollment change, Trial termination, Trial primary completion date: Phase IIb Study of PRO045 in Subjects With Duchenne Muscular Dystrophy (clinicaltrials.gov) - Oct 28, 2016 P2b, N=15, Terminated, N=45 --> 9 | Active, not recruiting --> Terminated N=45 --> 15 | Active, not recruiting --> Terminated | Trial primary completion date: Jul 2016 --> Jul 2017
- |||||||||| Trial primary completion date: Stem Cell Therapy in Muscular Dystrophy (clinicaltrials.gov) - Sep 26, 2016
P1, N=1000, Recruiting, Recruiting --> Completed | N=30 --> 20 | Trial primary completion date: Jan 2014 --> Apr 2014 Trial primary completion date: Jan 2016 --> Dec 2017
- |||||||||| Trial completion, Enrollment change, Trial initiation date, Trial primary completion date: Cell Therapy in Limb Girdle Muscular Dystrophy (clinicaltrials.gov) - Sep 26, 2016
P1, N=65, Completed, Trial primary completion date: Jan 2016 --> Dec 2017 Recruiting --> Completed | N=200 --> 65 | Initiation date: Dec 2013 --> Dec 2010 | Trial primary completion date: Dec 2015 --> Jan 2015
- |||||||||| Trial completion, Enrollment change: Stem Cell Therapy in Duchenne Muscular Dystrophy (clinicaltrials.gov) - Sep 26, 2016
P1, N=245, Completed, Recruiting --> Completed | N=200 --> 65 | Initiation date: Dec 2013 --> Dec 2010 | Trial primary completion date: Dec 2015 --> Jan 2015 Recruiting --> Completed | N=500 --> 245
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