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7 Companies |
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4 Products |
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4 Products |
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6 Mechanisms of Action |
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0 Trials |
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12 News |
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- | Trial completion: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders (clinicaltrials.gov) - Feb 5, 2018
P2, N=46, Completed, Sponsor: Masonic Cancer Center, University of Minnesota
Active, not recruiting --> Completed
- Enrollment change: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders (clinicaltrials.gov) - Jan 25, 2016
P2, N=46, Active, not recruiting, Sponsor: Masonic Cancer Center, University of Minnesota
Active, not recruiting --> Completed N=66 --> 46
- | Trial completion, Enrollment change, Trial primary completion date: Screening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy Syndrome (clinicaltrials.gov) - Aug 13, 2015
P=N/A, N=17, Completed, Sponsor: Greenwood Genetic Center
N=66 --> 46 Enrolling by invitation --> Completed | N=90 --> 17 | Trial primary completion date: Oct 2014 --> May 2014
- | Trial completion, Enrollment change, Trial primary completion date: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease (clinicaltrials.gov) - Aug 12, 2015
P=N/A, N=22, Completed, Sponsor: Children's Hospitals and Clinics of Minnesota
Enrolling by invitation --> Completed | N=90 --> 17 | Trial primary completion date: Oct 2014 --> May 2014 Recruiting --> Completed | N=50 --> 22 | Trial primary completion date: Apr 2014 --> Jun 2015
- Enrollment closed, Trial primary completion date: Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders (clinicaltrials.gov) - Apr 25, 2015
P2, N=66, Active, not recruiting, Sponsor: Masonic Cancer Center, University of Minnesota
Recruiting --> Completed | N=50 --> 22 | Trial primary completion date: Apr 2014 --> Jun 2015 Recruiting --> Active, not recruiting | Trial primary completion date: Nov 2014 --> Jun 2015
- Trial termination: UCBT-002: ALD-101 Adjuvant Therapy of Unrelated Umbilical Cord Blood Transfusion (UCBT) in Patients With Inherited Metabolic Diseases (clinicaltrials.gov) - Jul 8, 2014
P3, N=40, Terminated, Sponsor: Aldagen
Recruiting --> Active, not recruiting | Trial primary completion date: Nov 2014 --> Jun 2015 Suspended --> Terminated; Terminated - Sponsor Decision
- || Enrollment change: Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02 (clinicaltrials.gov) - Mar 30, 2014
P=N/A, N=59, Completed, Sponsor: BioMarin Pharmaceutical
Suspended --> Terminated; Terminated - Sponsor Decision N=80 --> 59
- ||| Trial completion: Observational Study of Patients With Mucopolysaccharidosis (MPS) VI Who Previously Participated in ASB-00-02 (clinicaltrials.gov) - Mar 30, 2014
P=N/A, N=59, Completed, Sponsor: BioMarin Pharmaceutical
N=80 --> 59 Enrolling by invitation --> Completed
- || NN1213 / Novo Nordisk
Trial completion: Study of rhASB in Patients With Mucopolysaccharidosis VI (clinicaltrials.gov) - Feb 22, 2014
P3, N=39, Completed, Sponsor: BioMarin Pharmaceutical
Enrolling by invitation --> Completed No longer recruiting --> Completed
- NN1213 / Novo Nordisk
Trial completion: Open-Label Study of Efficacy and Safety of Recombinant Human N-acetylgalactosamine 4-sulfatase in Patients With MPS VI (clinicaltrials.gov) - Feb 22, 2014
P2, N=0, Completed, Sponsor: BioMarin Pharmaceutical
No longer recruiting --> Completed No longer recruiting --> Completed
- Trial termination: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics (clinicaltrials.gov) - May 22, 2013
P=N/A, N=3000, Terminated, Sponsor: National MPS Society
No longer recruiting --> Completed Recruiting --> Terminated; Funding withdrawn due to insufficient enrollment rate
- Clinical: Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease (clinicaltrials.gov) - Oct 14, 2012
P=N/A, N=50, Recruiting, Sponsor: Children's Hospitals and Clinics of Minnesota