Mucopolysaccharidosis Type IIIA
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 2 Companies   1 Product   1 Product   4 Mechanisms of Action   0 Trials   11 News 
  • ||||||||||  Trial completion:  Natural History Studies of Mucopolysaccharidosis III (clinicaltrials.gov) -  Nov 16, 2015   
    P=N/A,  N=25, Completed, 
    Initiation date: Oct 2013 --> May 2013 | Trial primary completion date: Jun 2017 --> May 2016 Recruiting --> Completed
  • ||||||||||  Trial initiation date, Trial primary completion date:  Natural History Studies of Mucopolysaccharidosis III (clinicaltrials.gov) -  Feb 12, 2015   
    P=N/A,  N=30, Recruiting, 
    Trial primary completion date: Jun 2014 --> Jun 2017 Initiation date: Aug 2013 --> Feb 2014 | Trial primary completion date: Jul 2015 --> Oct 2015
  • ||||||||||  Enrollment open:  Natural History Studies of Mucopolysaccharidosis III (clinicaltrials.gov) -  Jan 14, 2014   
    P=N/A,  N=30, Recruiting, 
    Suspended --> Terminated; Terminated - Sponsor Decision Not yet recruiting --> Recruiting
  • ||||||||||  SAF-301 / Lysogene, Alcyone
    Trial completion, Gene therapy, Viral vector:  Intracerebral Gene Therapy for Sanfilippo Type A Syndrome (clinicaltrials.gov) -  Jul 8, 2013   
    P1/2,  N=4, Completed, 
    Not yet recruiting --> Recruiting Active, not recruiting --> Completed