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2 Companies |
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1 Product |
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1 Product |
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2 Mechanisms of Action |
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0 Trials |
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13 News |
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- | Vincerinone (vatiquinone) / Sumitomo Pharma, PTC Therap
Trial completion, Trial primary completion date: EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment (clinicaltrials.gov) - Apr 25, 2017
P2, N=30, Completed, Sponsor: Bambino Ges
Active, not recruiting --> Completed | Trial primary completion date: Jul 2014 --> Jul 2013
- Trial completion, Enrollment change: Pilot Study For Hypothermia Treatment In Hyperammonemic Encephalopathy In Neonates And Very Young Infants (clinicaltrials.gov) - Jun 1, 2015
P2, N=5, Completed, Sponsor: Uta Lichter-Konecki
Active, not recruiting --> Completed | Trial primary completion date: Jul 2014 --> Jul 2013 Recruiting --> Completed | N=24 --> 5
- Enrollment change, Trial termination, Trial primary completion date: Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia (clinicaltrials.gov) - Feb 5, 2015
P2, N=1, Terminated, Sponsor: Mendel Tuchman
Recruiting --> Completed | N=24 --> 5 N=34 --> 1 | Recruiting --> Terminated | Trial primary completion date: Mar 2016 --> Feb 2015; insufficient enrollment
- Trial primary completion date: Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate (clinicaltrials.gov) - May 27, 2014
P2, N=0, Withdrawn, Sponsor: Children's Hospital of Philadelphia
N=34 --> 1 | Recruiting --> Terminated | Trial primary completion date: Mar 2016 --> Feb 2015; insufficient enrollment Trial primary completion date: Jun 2016 --> Aug 2012
- Trial withdrawal: Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate (clinicaltrials.gov) - May 27, 2014
P2, N=0, Withdrawn, Sponsor: Children's Hospital of Philadelphia
Trial primary completion date: Jun 2016 --> Aug 2012 Recruiting --> Withdrawn
- Trial completion date: Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate (clinicaltrials.gov) - May 27, 2014
P2, N=0, Withdrawn, Sponsor: Children's Hospital of Philadelphia
Recruiting --> Withdrawn Trial completion date: Jun 2016 --> Aug 2012
- Enrollment change: Increasing Ureagenesis in Inborn Errors of Metabolism With N-Carbamylglutamate (clinicaltrials.gov) - May 27, 2014
P2, N=0, Withdrawn, Sponsor: Children's Hospital of Philadelphia
Trial completion date: Jun 2016 --> Aug 2012 N=80 --> 0
- Vincerinone (vatiquinone) / Sumitomo Pharma, PTC Therap
Enrollment closed: EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment (clinicaltrials.gov) - Apr 22, 2014
P2, N=30, Active, not recruiting, Sponsor: Bambino Ges
N=80 --> 0 Recruiting --> Active, not recruiting
- Enrollment open: Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia (clinicaltrials.gov) - Sep 2, 2013
P2, N=34, Recruiting, Sponsor: Children's Research Institute
Recruiting --> Active, not recruiting Not yet recruiting --> Recruiting
- Vincerinone (vatiquinone) / Sumitomo Pharma, PTC Therap
New P2 trial: EPI-743 in Cobalamin C Defect: Effects on Visual and Neurological Impairment (clinicaltrials.gov) - Feb 13, 2013
P2, N=30, Active, not recruiting, Sponsor: Bambino Ges
- New P2 trial: Pilot Study For Hypothermia Treatment In Hyperammonemic Encephalopathy In Neonates And Very Young Infants (clinicaltrials.gov) - Jun 18, 2012
P2, N=24, Recruiting, Sponsor: Children's Research Institute
- New P2 trial: Long-term Outcome of N-Carbamylglutamate Treatment in Propionic Acidemia and Methylmalonic Acidemia (clinicaltrials.gov) - May 10, 2012
P2, N=34, Recruiting, Sponsor: Children's Research Institute