Diseases
Companies
Products
Productz
Mechanisms of Action
Sites
Adenosine Deaminase Deficiency
Welcome,
Profile
Billing
Logout
0 Companies
0 Products
0 Products
0 Mechanisms of Action
1 Trial
4 News
||||||||||
Trial completion, Enrollment change, Gene therapy:
Gene Therapy ADA Deficiency
(clinicaltrials.gov) - Sep 15, 2015
P1/2
, N=8, Completed,
Sponsor: Great Ormond Street Hospital for Children NHS Foundation Trust
Recruiting --> Completed | N=10 --> 8
||||||||||
Enrollment change, Viral vector:
Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+ Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector
(clinicaltrials.gov) - Apr 14, 2015
P1
, N=1, Completed,
Sponsor: National Human Genome Research Institute (NHGRI)
Recruiting --> Completed | N=10 --> 8 N=10 --> 1
||||||||||
Trial completion, Trial primary completion date, Viral vector:
Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+ Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector
(clinicaltrials.gov) - Oct 10, 2014
P1
, N=10, Completed,
Sponsor: National Human Genome Research Institute (NHGRI)
N=10 --> 1 Recruiting --> Completed | Trial primary completion date: Mar 2016 --> Dec 2013
||||||||||
New P1 trial, Viral vector:
Treatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+ Cells After Addition of a Normal Human ADA cDNA by the EFS-ADA Lentiviral Vector
(clinicaltrials.gov) - Dec 26, 2013
P1
, N=10, Recruiting,
Sponsor: National Human Genome Research Institute (NHGRI)