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DT-DEC01 (MB^N/MB^DMD DEC), DT-DEC01, Suspension for injection

Dystrogen Therapeutics Technology Polska Spółka z Ograniczoną Odpowiedzialnością, Dystrogen Therapeutics Technology Polska Spółka z Ograniczoną Odpowiedzialnością

Duchenne muscular dystrophy (DMD) is the most common inherited neuromuscular disease that mostly affects boys. DMD is a type of X-linked disease caused by a mutation of the gene at the Xp21 locus that encodes the dystrophin protein, resulting in a complete lack of this protein in the muscles of affected boys. DMD is characterized by skeletal and cardiac muscle degeneration. Most DMD-affected boys lose their ability to walk by the age of 10-14., Duchenne muscular dystrophy (DMD) is the most common inherited neuromuscular disease that mostly affects boys. DMD is characterized by skeletal and cardiac muscle degeneration., Diseases [C] - Musculoskeletal Diseases [C05]