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7 Trials

   

Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Viltepso (viltolarsen) / Nippon Shinyaku, National Center of Neurology and Psychiatry
NCT04687020: Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)

Active, not recruiting
4
9
Canada, US
Viltolarsen
NS Pharma, Inc.
Duchenne Muscular Dystrophy
09/32
10/32
NCT04060199 / 2019-002076-13: Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)

Completed
3
77
Europe, Canada, US, RoW
Viltolarsen, NS-065/NCNP-01, Placebo
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
10/23
10/23
NCT04768062 / 2021-000122-10: Study to Assess the Safety and Efficacy of Viltolarsen in Ambulant Boys With DMD (RACER53-X)

Active, not recruiting
3
74
Europe, Canada, Japan, RoW
Viltolarsen, NS-065/NCNP-01
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
10/25
11/25
Galactic53, NCT04956289 / 2020-003653-30: Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD

Completed
2
20
Europe, US, RoW
Viltolarsen, NS-065/NCNP-01
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
06/23
07/23
brogidirsen (NS-089/NCNP-02) / Nippon Shinyaku, National Center of Neurology and Psychiatry
NCT05996003: NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

Recruiting
2
20
US
NS-089/NCNP-02, Brogidirsen
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
09/26
09/26
NCT05135663: Extension Study of NS-089/NCNP-02 in DMD

Active, not recruiting
2
6
Japan
NS-089/NCNP-02
Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy (DMD)
01/26
07/26
OCH-NCNP1 / Eisai
NCT04211740: Phase II Clinical Trial of OCH-NCNP1

Completed
2
30
Japan
OCH-NCNP1, Placebo
National Center of Neurology and Psychiatry, Japan
Multiple Sclerosis, Relapsing-Remitting, Multiple Sclerosis, Secondary Progressive
05/23
05/23
Trial + Data / EventsStatusPhNRegionInterventionsSponsorConditionsPrimary complStudy compl
Viltepso (viltolarsen) / Nippon Shinyaku, National Center of Neurology and Psychiatry
NCT04687020: Long-term Use of Viltolarsen in Boys With Duchenne Muscular Dystrophy in Clinical Practice (VILT-502)

Active, not recruiting
4
9
Canada, US
Viltolarsen
NS Pharma, Inc.
Duchenne Muscular Dystrophy
09/32
10/32
NCT04060199 / 2019-002076-13: Study to Assess the Efficacy and Safety of Viltolarsen in Ambulant Boys With DMD (RACER53)

Completed
3
77
Europe, Canada, US, RoW
Viltolarsen, NS-065/NCNP-01, Placebo
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
10/23
10/23
NCT04768062 / 2021-000122-10: Study to Assess the Safety and Efficacy of Viltolarsen in Ambulant Boys With DMD (RACER53-X)

Active, not recruiting
3
74
Europe, Canada, Japan, RoW
Viltolarsen, NS-065/NCNP-01
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
10/25
11/25
Galactic53, NCT04956289 / 2020-003653-30: Study to Assess the Safety, Tolerability, and Efficacy of Viltolarsen in Ambulant and Non-Ambulant Boys With DMD

Completed
2
20
Europe, US, RoW
Viltolarsen, NS-065/NCNP-01
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
06/23
07/23
brogidirsen (NS-089/NCNP-02) / Nippon Shinyaku, National Center of Neurology and Psychiatry
NCT05996003: NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

Recruiting
2
20
US
NS-089/NCNP-02, Brogidirsen
NS Pharma, Inc., Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy
09/26
09/26
NCT05135663: Extension Study of NS-089/NCNP-02 in DMD

Active, not recruiting
2
6
Japan
NS-089/NCNP-02
Nippon Shinyaku Co., Ltd.
Duchenne Muscular Dystrophy (DMD)
01/26
07/26
OCH-NCNP1 / Eisai
NCT04211740: Phase II Clinical Trial of OCH-NCNP1

Completed
2
30
Japan
OCH-NCNP1, Placebo
National Center of Neurology and Psychiatry, Japan
Multiple Sclerosis, Relapsing-Remitting, Multiple Sclerosis, Secondary Progressive
05/23
05/23

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