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 50 Products   109 Diseases   50 Products   100 Trials   15044 News 

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 Trials
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Incivek (telaprevir) / J&J, Vertex, Mitsubishi Tanabe           
          
            
             
Kalydeco (ivacaftor) / Vertex           
          
            
             
Trikafta (elexacaftor/tezacaftor/ivacaftor) / Vertex           
          
            
             
Orkambi (lumacaftor/ivacaftor) / Vertex           
          
            
             
berzosertib (M6620) / EMD Serono           
          
            
             
Symdeko (tezacaftor/ivacaftor) / Vertex           
          
            
             
suzetrigine (VX-548) / Vertex           
          
            
             
Casgevy (exagamglogene autotemcel) / Vertex, CRISPR Therap, Molecular Templates           
          
            
             
vanzacaftor/tezacaftor/deutivacaftor (VX-121/VX-661/VX-561) / Vertex           
          
            
             
tozasertib (MK-0457) / Merck (MSD)           
          
            
             
deutivacaftor (VX-561) / Vertex           
          
            
             
bamocaftor (VX-659) / Vertex           
          
            
             
decernotinib (VX-509) / Vertex           
          
            
             
VX-150 / Vertex           
          
            
             
belnacasan (VX-765) / Vertex           
          
            
             
idrevloride (P-1037) / Parion Sciences           
          
            
             
inaxaplin (VX-147) / Vertex           
          
            
             
lomibuvir (VX 222) / Trek Therapeutics           
          
            
             
lumacaftor (VX-809) / Vertex           
          
            
             
ALS-2200 / J&J, Vertex, BMS           
          
            
             
vanzacaftor (VX-121) / Vertex           
          
            
             
PEC-Encap (encapsulated human islet cell therapy) / Vertex           
          
            
             
VX-864 / Vertex           
          
            
             
elexacaftor (VX-445) / Vertex           
          
            
             
gartisertib (M4344) / EMD Serono           
          
            
             
ALS-2158 / J&J, Vertex           
          
            
             
PEC-Direct (PEC-01) / Vertex           
          
            
             
VX-708 / Vertex           
          
            
             
VX-814 / Vertex           
          
            
             
VX-993 / Vertex           
          
            
             
olacaftor (VX-440) / Vertex           
          
            
             
tezacaftor (VX-661) / Vertex           
          
            
             
CTX211 / CRISPR Therap, Vertex           
          
            
             
M9831 / EMD Serono           
          
            
             
MK-5108 / Vertex, Merck (MSD)           
          
            
             
PEC-QT / CRISPR Therap, Vertex           
          
            
             
VCH 916 / Vertex           
          
            
             
VTX-11e / Vertex, National Institutes of Health           
          
            
             
VX 759 / Vertex           
          
            
             
VX-152 / Vertex           
          
            
             
VX-522 / Vertex, Moderna           
          
            
             
VX-634 / Vertex           
          
            
             
VX-668 / Vertex           
          
            
             
VX-840 / Vertex           
          
            
             
VX-880 / Vertex