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Talzenna
(talazoparib) / Pfizer
Palynziq
(pegvaliase-pqpz) / BioMarin
Voxzogo
(vosoritide) / BioMarin
Vimizim
(elosulfase alfa) / BioMarin
Kyndrisa
(drisapersen) / BioMarin
Roctavian
(valoctocogene roxaparvovec-rvox) / BioMarin
reveglucosidase alfa
(BMN 701) / BioMarin