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20 Products
84 Diseases
20 Products
98 Trials
4421 News
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Phase
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1
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Trials
0
13
26
39
52
65
78
91
104
117
130
Talzenna
(talazoparib) / Pfizer
sapropterin
/ Generic mfg.
Aldurazyme
(laronidase) / BioMarin, Sanofi
Palynziq
(pegvaliase-pqpz) / BioMarin
Voxzogo
(vosoritide) / BioMarin
Firdapse
(amifampridine) / BioMarin, Catalyst Pharma
Vimizim
(elosulfase alfa) / BioMarin
Kyndrisa
(drisapersen) / BioMarin
Roctavian
(valoctocogene roxaparvovec-rvox) / BioMarin
Brineura
(cerliponase alfa) / BioMarin
Naglazyme
(galsulfase) / AnGes MG, BioMarin
tralesinidase alfa
(AX 250) / Allievex Corp
BMN 044
/ BioMarin
reveglucosidase alfa
(BMN 701) / BioMarin
BMN 331
/ BioMarin
domofenogene zalfaparvovec
(BMN 307) / BioMarin
BMN 045
/ BioMarin
BMN 053
/ BioMarin
BMN 255
/ BioMarin
BMN 349
/ BioMarin
BMN 351
/ BioMarin