Ultragenyx 
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 14 Products   3 Diseases   14 Products   31 Trials   3169 News 

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 Trials
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Dojolvi (triheptanoin) / Ultragenyx           
          
            
             
Crysvita (burosumab-twza) / Ultragenyx, Kyowa Kirin           
          
            
             
Evkeeza (evinacumab-dgnb) / Regeneron           
          
            
             
setrusumab (UX143) / Mereo Biopharma, Ultragenyx           
          
            
             
sialic acid extended release (SA-ER) / Ultragenyx, Nobelpharma           
          
            
             
Mepsevii (vestronidase alfa) / Ultragenyx, Amicus           
          
            
             
rebisufligene etisparvovec (UX111) / Ultragenyx           
          
            
             
apazunersen (GTX-102) / Foundation for Angelman Syndrome Therap, Ultragenyx           
          
            
             
avalotcagene ontaparvovec (DTX301) / Ultragenyx           
          
            
             
DTX101 / Ultragenyx           
          
            
             
UX053 / Ultragenyx, Arcturus Therap           
          
            
             
pariglasgene brecaparvovec (DTX401) / Ultragenyx           
          
            
             
peboctocogene camaparvovec (DTX201) / Ultragenyx           
          
            
             
rivunatpagene miziparvovec (UX701) / Ultragenyx